New aspects of myofibrillar myopathies
RA Kley, M Olivé, R Schröder - Current Opinion in Neurology, 2016 - journals.lww.com
RA Kley, M Olivé, R Schröder
Current Opinion in Neurology, 2016•journals.lww.comMFMs are an expanding and numerically significant group of protein aggregate diseases
with marked clinical and genetic heterogeneity. Though no specific therapy is currently
available, the generation of patient-mimicking cell and animal models now paves the way for
the preclinical evaluation of novel therapeutic strategies.
with marked clinical and genetic heterogeneity. Though no specific therapy is currently
available, the generation of patient-mimicking cell and animal models now paves the way for
the preclinical evaluation of novel therapeutic strategies.
Summary
MFMs are an expanding and numerically significant group of protein aggregate diseases with marked clinical and genetic heterogeneity. Though no specific therapy is currently available, the generation of patient-mimicking cell and animal models now paves the way for the preclinical evaluation of novel therapeutic strategies.
Lippincott Williams & Wilkins